questionText: To ask the Secretary of State for Health and Social Care, what assessment his Department has made of the adequacy of appraisal processes for (a) Freidrich’s Ataxia, (b) Neiman Pick’s disease and (c) other rare diseases for exceptional conditions.
answerText: The National Institute for Health and Care Excellence’s (NICE) methods have been proven to be suitable for the evaluation of rare disease medicines, where companies are willing to price their medicines fairly. NICE’s approval rate for medicines for rare d...
heading: Rare Diseases: Medical Treatments